New gene therapies may soon treat dozens of rare diseases, but million-dollar price tags will put them out of reach for many
New payment models may mean more of the people who need these treatments can get them.
Kevin Doxzen, Hoffmann Postdoctoral Fellow, Arizona State University •
conversation
Aug. 31, 2021 • ~8 min
Aug. 31, 2021 • ~8 min
Researchers unveil stem cell models of human spine development
Harvard researchers have unveiled the first stem cell models of human spine development, setting the stage for better understanding of musculoskeletal and metabolic disorders, including congenital scoliosis, muscular dystrophy, and Type 2 diabetes.
Stephanie Dutchen
• harvard
Jan. 8, 2020 • ~6 min
Jan. 8, 2020 • ~6 min
Exercise, fasting shown to help cells shed defective proteins
A new study from the Blavatnik Institute finds that intense exercise and fasting activate hormones that boost cells’ capacity to dispose of defective proteins, which clog up the cell, interfere with its functions, and, over time, precipitate diseases including neurodegenerative conditions such as ALS and Alzheimer’s.
Ekaterina Pesheva
• harvard
Feb. 21, 2019 • ~9 min
Feb. 21, 2019 • ~9 min
/
1