A team of researchers has developed a new drug delivery system that was able to edit genes associated with high cholesterol and to partially restore vision in mice.

Single-cell gene expression analyses of human cerebrovascular cells can help reveal new drug targets for Huntington’s disease.

The technique can help predict a cell’s path over time, such as what type of cell it will become.

A new study finds the clusters form small, stable droplets and may give the genome a gel-like structure.

While the brain acquires resistance to continuous treatment with mGluR5 inhibitor drugs, lasting effects may still arise if dosing occurs intermittently and during a developmental-critical period.

Neural network identifies synergistic drug blends for treating viruses like SARS-CoV-2.

Researchers find RNA-guided enzymes are more diverse and widespread than previously believed.

Made of components found in the human body, the programmable system is a step toward safer, targeted delivery of gene editing and other molecular therapeutics.

A Harvard study could lead to potential therapeutics for one of the most prominent ailments of the elderly and one of the most prominent musculoskeletal defects in newborns.

Scientists at Harvard and the Broad Institute have demonstrated that it is possible to treat sickle cell disease in mice using a new gene-editing technique.