A better gene-transport system targets diseased muscle tissue

A newly engineered gene-delivery system has the potential to make gene therapy for muscle diseases both safer and more effective for patients.

Juan Siliezar • harvard
Oct. 19, 2021 • ~8 min

Progeria study finds base-editing therapy lengthens lifespan in mice

Several hundred children worldwide live with progeria, a deadly premature aging disease.

Caitlin McDermott-Murphy • harvard
Jan. 27, 2021 • ~9 min

Gene editing may be a path to restore partial hearing

Wei Hsi “Ariel” Yeh dedicated her research in chemistry to solving some of the vast genetic mysteries behind hearing loss.

Caitlin McDermott-Murphy • harvard
June 5, 2020 • ~6 min

Removing the constraining requirements at gene editing site

Investigators at Massachusetts General Hospital have modified the gene editing system, making it possible to potentially target any location across the entire human genome.

Harvard Gazette • harvard
March 26, 2020 • ~3 min

How CRISPR technology is advancing

Fewer off-target edits and greater targeting scope bring gene editing technology closer to treating human diseases.

Caitlin McDermott-Murphy • harvard
Feb. 14, 2020 • ~7 min

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