A better gene-transport system targets diseased muscle tissue

A newly engineered gene-delivery system has the potential to make gene therapy for muscle diseases both safer and more effective for patients.

Juan Siliezar • harvard
Oct. 19, 2021 • ~8 min

Major study on Duchenne muscular dystrophy gains support

Harvard stem-cell research receives support from Sarepta Therapeutics for work on Duchenne muscular dystrophy.

Caroline Perry • harvard
Jan. 9, 2020 • ~6 min

Breakthrough Harvard research shows stem cell genes can be edited in living systems

Study shows how genes could be edited in stem cells within intact organs, without having to remove them from their normal environment. The new approach could treat a variety of diseases.

Mary Todd Bergman • harvard
June 4, 2019 • ~6 min

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